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  1. Galafold® (migalastat) | Official Patient Site

    Some things need a lot of time. A pill for Fabry disease isn’t one of them. Galafold is the first and only oral therapy for adults with Fabry disease and an amenable GLA variant. Learn about …

  2. Understanding Galafold: How This Oral Treatment Works for Fabry Disease

    This is the first and only medicine for Fabry disease that can be taken by mouth. Other treatments for Fabry disease, called enzyme replacement therapy, are injected into the body.

  3. Amicus' oral Fabry disease drug approved in US - pharmaphorum

    4 days ago · Galafold (migalastat) is an oral precision medicine for adults with a confirmed diagnosis of Fabry disease and an amenable galactosidase alpha gene variant, based on in …

  4. Galafold: A Targeted Therapy for Fabry Disease

    Oct 30, 2025 · What Is Galafold? Galafold (migalastat) is a prescription oral medication used to treat adults with Fabry disease who have a confirmed “amenable” GLA gene mutation. …

  5. About Galafold® (migalastat) | Oral Precision Medicine

    For adults with confirmed Fabry disease and an amenable GLA variant Galafold—the first oral precision medicine for Fabry disease Alex, living with Fabry disease

  6. Galafold (migalastat) for Fabry disease

    Mar 6, 2024 · Galafold is an approved oral therapy for adults with Fabry disease and amenable mutations that helps to clear cells of toxic fatty molecules.

  7. What is the Oral Treatment for Fabry Disease? (Galafold)

    4 days ago · The oral treatment for Fabry disease is migalastat (Galafold), a chaperone therapy for adults with specific 'amenable' GLA mutations. Learn how it works and who is eligible.

  8. Galafold - Rare Disease Advisor

    Galafold ® (migalastat) is an oral prescription medicine indicated for the treatment of adults with Fabry disease who have a responsive galactosidase alpha (GLA) gene variant, as determined …

  9. Migalastat: A Review in Fabry Disease - PMC

    Fabry disease is a rare lysosomal disorder characterized by deficient or absent α-galactosidase A activity resulting from mutations in the GLA gene. Migalastat (Galafold™), a pharmacological …

  10. What is Galafold? Galafold® (migalastat) is a prescription medicine used to treat adults with Fabry disease who have a certain genetic change (variant) in the galactosidase alpha gene (GLA) …