Michigan's health department announced a new plan to improve care and support for the 4,000 residents with sickle cell disease.

AND017 is an investigational oral hypoxia-inducible factor prolyl hydroxylase inhibitor. The Food and Drug Administration has granted Orphan Drug designation to KIND Pharmaceutical’s AND017 for the ...

SOMERVILLE, Mass.--(BUSINESS WIRE)--bluebird bio, Inc. (NASDAQ: BLUE) (“bluebird bio” or “bluebird”) today announced new and updated efficacy, safety and health-related quality of life (HRQoL) data ...

Nemours Children's Hospital is now offering Lyfgenia gene therapy. The treatment aims to reduce pain crises and hospital visits for young patients.

It’s a medical breakthrough in treating sickle cell disease and a Michigan man is proof that it works.

Chantez Sanford Jr., 24, of Southfield, says his life has been transformed after undergoing Lyfgenia gene therapy at Children ...

Beam Therapeutics’ experimental gene-editing therapy for sickle cell disease now has its first cut of patient data showing signs of treating the rare blood disorder in a way that could differentiate ...

Sickle Cell Anemia is a genetic blood disorder that affects the shape and function of red blood cells. It can lead to severe health complications, including pain, infections, and anemia. Understanding ...

The federal approval of two new gene therapy treatments for sickle cell disease has created a groundbreaking option for patients. Across the nation, it is unknown how many suffer from the disease, but ...

Gene therapy has the potential to dramatically benefit patients with genetic blood disorders, but a small study on participants in a clinical trial for sickle cell disease suggests that a key process ...

Today is World Sickle Cell Disease Day. The international awareness day is observed annually to increase public knowledge and an understanding of sickle cell disease and the challenges experienced by ...